Search Result "rAAV"


Retinal Ganglion Cell Gene Therapy and Visual System Repair

Journal: Current Gene Therapy
Volume: 11 Issue: 2 Year: 2011 Page: 116-131
Author(s): Mats Hellstrom, Alan R. Harvey

Adeno-Associated Virus (AAV) Vectors in the CNS

Journal: Current Gene Therapy
Volume: 11 Issue: 3 Year: 2011 Page: 181-188
Author(s): Thomas J. McCown

Atherosclerosis, Degenerative Aortic Stenosis and Statins

Journal: Current Drug Targets
Volume: 12 Issue: 1 Year: 2011 Page: 115-121
Author(s): Giuseppina Novo, Giovanni Fazio, Claudia Visconti, Patrizia Carita, Ermanno Maira, Khalil Fattouch, Salvatore Novo

Current Options and Future Possibilities for the Treatment of Dyskinesia and Motor Fluctuations in Parkinsons Disease

Journal: CNS & Neurological Disorders - Drug Targets
Volume: 10 Issue: 6 Year: 2011 Page: 670-684
Author(s): M. A. Cenci, K. E. Ohlin, P. Odin

Treatment of Fabry Disease: Current and Emerging Strategies

Journal: Current Pharmaceutical Biotechnology
Volume: 12 Issue: 6 Year: 2011 Page: 916-922
Author(s): Paula Rozenfeld, Pablo M. Neumann

GDNF Family Ligands: A Potential Future for Parkinsons Disease Therapy

Journal: CNS & Neurological Disorders - Drug Targets
Volume: 10 Issue: 6 Year: 2011 Page: 703-711
Author(s): Amanda L. Mickiewicz, Jeffrey H. Kordower

Cell-and Gene-based Therapeutic Approaches for Neurological Deficits in Mucopolysaccharidoses

Journal: Current Pharmaceutical Biotechnology
Volume: 12 Issue: 6 Year: 2011 Page: 884-896
Author(s): Dao Pan

Retinitis Pigmentosa: Genes and Disease Mechanisms

Journal: Current Genomics
Volume: 12 Issue: 4 Year: 2011 Page: 238-249
Author(s): Francesco Parmeggiani, Francesco S. Sorrentino, Diego Ponzin, Vanessa Barbaro, Stefano Ferrari, Enzo Di Iorio

Adeno-associated Viral Vectors for Correction of Inborn Errors of Metabolism: Progressing Towards Clinical Application

Journal: Current Pharmaceutical Design
Volume: 17 Issue: 2 Year: 2011 Page: 2500-2515
Author(s): Frank Jacobs, Lili Wang

Immune Responses to AAV in Clinical Trials

Journal: Current Gene Therapy
Volume: 11 Issue: 4 Year: 2011 Page: 321-330
Author(s): Federico Mingozzi, Katherine A. High

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