Search Result "dystrophy"


Therapeutic Approaches for Dominant Muscle Diseases: Highlight on Myotonic Dystrophy

Journal: Current Gene Therapy
Volume: 15 Issue: 4 Year: 2015 Page: 329-337
Author(s): A. F. Klein,S. Dastidar,D. Furling,M. K. Chuah

Adeno-Associated Virus (AAV) Mediated Dystrophin Gene Transfer Studies and Exon Skipping Strategies for Duchenne Muscular Dystrophy (DMD)

Journal: Current Gene Therapy
Volume: 15 Issue: 4 Year: 2015 Page: 395-415
Author(s): Klaudia Kawecka,Michael Theodoulides,Yalin Hasoglu,Susan Jarmin,Hanna Kymalainen,Anita Le-Heron,Linda Popplewell,Alberto Malerba,George Dickson,Takis Athanasopoulos

Pluripotent Stem Cells for Gene Therapy of Degenerative Muscle Diseases

Journal: Current Gene Therapy
Volume: 15 Issue: 4 Year: 2015 Page: 364-380
Author(s): Mariana Loperfido,Heather B. Steele-Stallard,Francesco Saverio Tedesco,Thierry VandenDriessche

Biology and Regulatory Roles of Nuclear Lamins in Cellular Function and Dysfunction

Journal: Recent Patents on Endocrine, Metabolic & Immune Drug Discovery
Volume: 9 Issue: 2 Year: 2015 Page: 111-120
Author(s): Syeda G. Khadija,Fei Chen,Timothy Hadden,Randall L. Commissaris,Anjaneyulu Kowluru

Stem Cell-Mediated Exon Skipping of the Dystrophin Gene by the Bystander Effect

Journal: Current Gene Therapy
Volume: 15 Issue: 6 Year: 2015 Page: 563-571
Author(s): Mirella Meregalli,Andrea Farini,Clementina Sitzia,Cyriaque Beley,Paola Razini,Letizia Cassinelli,Federica Colleoni,Paola Frattini,Nadia Santo,Elisabetta Galbiati,Davide Prosperi,Alessandro Tavelli,Marzia Belicchi,Luis Garcia,Yvan Torrente

Adult Stem Cells and Skeletal Muscle Regeneration

Journal: Current Gene Therapy
Volume: 15 Issue: 4 Year: 2015 Page: 348-363
Author(s): Domiziana Costamagna,Emanuele Berardi,Gabriele Ceccarelli,Maurilio Sampaolesi

Antisense Therapy for Cardiovascular Diseases

Journal: Current Pharmaceutical Design
Volume: 21 Issue: 30 Year: 2015 Page: 4417-4426
Author(s): M. Ian Phillips,Jessica Costales,Robert J. Lee,Edilamar Oliveira,Andrew B. Burns

The Proteolytic Systems of Muscle Wasting

Journal: Recent Advances in DNA & Gene Sequences (Discontinued)
Volume: 9 Issue: 1 Year: 2015 Page: 26-35
Author(s): Bianca Maria Scicchitano,Martina Faraldi,Antonio Musarò

Editorial free to download

Editorial (Thematic Issue):Stem Cell-Based and Gene Therapy for Hereditary Muscle Disorders

Journal: Current Gene Therapy
Volume: 15 Issue: 4 Year: 2015 Page: 327-328
Author(s): Marinee K. Chuah

Mouse Models of Experimental Autoimmune Uveitis: Comparative Analysis of Adjuvant-Induced vs Spontaneous Models of Uveitis

Journal: Current Molecular Medicine
Volume: 15 Issue: 6 Year: 2015 Page: 550-557
Author(s): J. Chen,H. Qian,R. Horai,C.-C. Chan,R.R. Caspi

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