Search Result "corrector"


Review Article

RNF5, DAB2 and Friends: Novel Drug Targets for Cystic Fibrosis

Journal: Current Pharmaceutical Design
Volume: 23 Issue: 1 Year: 2017 Page: 176-186
Author(s): Elvira Sondo,Emanuela Pesce,Valeria Tomati,Monica Marini,Nicoletta Pedemonte

Protein Misfolding in Disease and Small Molecule Therapies

Journal: Current Topics in Medicinal Chemistry
Volume: 12 Issue: 2 Year: 2012 Page: 2460-2469
Author(s): Claudio M. Gomes

Rescuing Mutant CFTR: A Multi-task Approach to a Better Outcome in Treating Cystic Fibrosis

Journal: Current Pharmaceutical Design
Volume: 19 Issue: 1 Year: 2013 Page: 3497-3508
Author(s): Margarida D. Amaral, Carlos M. Farinha

F508del-CFTR Rescue: A Matter of Cell Stress Response

Journal: Current Pharmaceutical Design
Volume: 19 Issue: 1 Year: 2013 Page: 3476-3496
Author(s): Erika Nieddu, Benedetta Pollarolo, Luisa Merello, Silvia Schenone, Mauro Mazzei

Pharmacological Correction of Cystic Fibrosis: Molecular Mechanisms at the Plasma Membrane to Augment Mutant CFTR Function

Journal: Current Drug Targets
Volume: 17 Issue: 11 Year: 2016 Page: 1275-1281
Author(s): Kavisha Arora,Anjaparavanda P. Naren

Identification and Validation of Hits from High Throughput Screens for CFTR Modulators

Journal: Current Pharmaceutical Design
Volume: 18 Issue: 5 Year: 2012 Page: 628-641
Author(s): Stan Pasyk, Steven Molinski, Wilson Yu, Paul D.W. Eckford, Christine E. Bear

New Genetic and Pharmacological Treatments for Cystic Fibrosis

Journal: Current Pediatric Reviews
Volume: 5 Issue: 1 Year: 2009 Page: 8-27
Author(s): Massimo Conese, Mario Romano, Maria Lucia Furnari, Elena Copreni, Ida De Fino, Francesca Pardo, Luis V. J. Galietta

On the Design of Broad Based Screening Assays to Identify Potential Pharmacological Chaperones of Protein Misfolding Diseases

Journal: Current Topics in Medicinal Chemistry
Volume: 12 Issue: 2 Year: 2012 Page: 2504-2522
Author(s): Subhashchandra Naik, Na Zhang, Phillip Gao, Mark T. Fisher

Targeting Molecular Chaperones for the Treatment of Cystic Fibrosis: Is It a Viable Approach?

Journal: Current Drug Targets
Volume: 16 Issue: 9 Year: 2015 Page: 958-964
Author(s): Ashley Heard,Jake Thompson,Jessica Carver,Michelle Bakey,X. Robert Wang

Novel Approaches for Potential Therapy of Cystic Fibrosis

Journal: Current Drug Targets
Volume: 16 Issue: 9 Year: 2015 Page: 923-936
Author(s): Victoria Sawczak,Paulina Getsy,Aliya Zaidi,Fei Sun,Khalequz Zaman,Benjamin Gaston

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