Search Result "Dp116"


General Research Article

Repurposing Pathogenic Variants of DMD Gene and its Isoforms for DMD Exon Skipping Intervention

Journal: Current Genomics
Volume: 20 Issue: 7 Year: 2019 Page: 519-530
Author(s): Rahul Tyagi,Sumit Kumar,Ashwin Dalal,Faruq Mohammed,Manju Mohanty,Paramvir Kaur,Akshay Anand

Blood-Brain Barrier Alterations in MDX Mouse, An Animal Model of the Duchenne Muscular Dystrophy

Journal: Current Neurovascular Research
Volume: 2 Issue: 1 Year: 2005 Page: 47-54
Author(s): Beatrice Nico, Luisa Roncali, Domenica Mangieri, Domenico Ribatti

Dystroglycan, A Multifunctional Adaptor Protein for Signal Transduction and A Potential Therapeutic Target

Journal: Current Signal Transduction Therapy
Volume: 6 Issue: 1 Year: 2011 Page: 71-81
Author(s): Hiroki Hagiwara, Kiichiro Matsumura

The Muscular Dystrophies Associated with Central Nervous System Lesions: A Brief Review from a Standpoint of the Localization and Function of Causative Genes

Journal: Current Pediatric Reviews
Volume: 10 Issue: 4 Year: 2014 Page: 282-291
Author(s): Tomoko Yamamoto,Atsuko Hiroi,Makiko Osawa,Noriyuki Shibata

Research Article

Lentiviral Micro-dystrophin Gene Treatment into Late-stage mdx Micefor Duchenne Muscular Dystrophy Disease

Journal: Current Gene Therapy
Volume: 23 Issue: 4 Year: 2023 Page: 304-315
Author(s): Selen Abanuz Eren,Kevser Buse Karadeniz,Raife Dilek Turan,Derya Dilek Kancagi,Sevdican Ustun Yilmaz,Ahmet Tarık Baykal

Personalised Genetic Intervention for Duchenne Muscular Dystrophy: Antisense Oligomers and Exon Skipping

Journal: Current Molecular Pharmacology
Volume: 2 Issue: 1 Year: 2009 Page: 110-121
Author(s): Chalermchai Mitrpant, Sue Fletcher, Steve D. Wilton

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