Current Gene Therapy


Liang Cheng
College of Bioinformatics Science and Technology
Harbin Medical University
Harbin, Heilongjiang

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Editor's Choice

Exosomes: Structure, Biogenesis, Types and Application in Diagnosis and Gene and Drug Delivery

Volume: 20   Issue: 3
Pp: 195-206
Shriya Agarwal, Vinayak Agarwal, Mugdha Agarwal and Manisha Singh*
DOI: 10.2174/1566523220999200731011702

Gene Therapy for Hemophilia A: Where We Stand

Volume: 20   Issue: 2
Pp: 142-151
Miaojin Zhou, Zhiqing Hu, Chunhua Zhang, Lingqian Wu, Zhuo Li* and Desheng Liang*
DOI: 10.2174/1566523220666200806110849

Artificial RNA Editing with ADAR for Gene Therapy

Volume: 20   Issue: 1
Pp: 44-54
Sonali Bhakta and Toshifumi Tsukahara*
DOI: 10.2174/1566523220666200516170137

Nano-enhanced Optical Gene Delivery to Retinal Degenerated Mice

Volume: 19   Issue: 5
Pp: 318-329
Subrata Batabyal, Sivakumar Gajjeraman, Sulagna Bhattacharya, Weldon Wright and Samarendra Mohanty*
DOI: 10.2174/1566523219666191017114044

Partial Reprogramming As An Emerging Strategy for Safe Induced Cell Generation and Rejuvenation

Volume: 19   Issue: 4
Pp: 248-254
Marianne Lehmann, Martina Canatelli-Mallat, Priscila Chiavellini, Gloria M. Cónsole, Maria D. Gallardo and Rodolfo G. Goya*
DOI: 10.2174/1566523219666190902154511

Reduction of Autophagic Accumulation in Pompe Disease Mouse Model Following Gene Therapy open access plus

Volume: 19   Issue: 3
Pp: 197-207
Angela L. McCall*, Sylvia G. Stankov, Gabrielle Cowen, Denise Cloutier, Zizhao Zhang, Lin Yang, Nathalie Clement, Darin J. Falk and Barry J. Byrne*
DOI: 10.2174/1566523219666190621113807

Three Cases of Leber’s Hereditary Optic Neuropathy with Rapid Increase in Visual Acuity After Gene Therapy open access plus

Volume: 19   Issue: 2
Pp: 134-138
Yong Zhang, Jia-jia Yuan, Hong-li Liu, Zhen Tian, Si-wei Liu and Bin Li*
DOI: 10.2174/1566523219666190618094505

Gene-based Therapeutic Tools in the Treatment of Cornea Disease

Volume: 19   Issue: 1
Pp: 7-19
Xiao-Xiao Lu and Shao-Zhen Zhao*
DOI: 10.2174/1566523219666181213120634

Neuroprotection by Human Dental Pulp Mesenchymal Stem Cells: From Billions to Nano

Volume: 18   Issue: 5
Pp: 307-323
Chaitra Venugopal, Shobha K, Kiranmai S. Rai, Venkata Bharatkumar Pinnelli, Bindu M. Kutty and Anandh Dhanushkodi*
DOI: 10.2174/1566523218666180913152615

Cellular, Molecular and Non-Pharmacological Therapeutic Advances for the Treatment of Parkinson's Disease: Separating Hope from Hype

Volume: 18   Issue: 4
Pp: 206-224
Mehdi Ghamgosha, Ali Mohammad Latifi, Gholam Hossein Meftahi and Alireza Mohammadi*
DOI: 10.2174/1566523218666180910163401

Gene Therapy to Enhance Bone and Cartilage Repair in Orthopaedic Surgery

Volume: 18   Issue: 3
Pp: 154-170
Sofia Bougioukli, Christopher H. Evans, Ram K. Alluri, Steven C. Ghivizzani and Jay R. Lieberman*
DOI: 10.2174/1566523218666180410152842

Dysfunction in Brain-Derived Neurotrophic Factor Signaling Pathway and Susceptibility to Schizophrenia, Parkinson’s and Alzheimer’s Diseases promotion: free to download

Volume: 18   Issue: 1
Pp: 45-63
Alireza Mohammadi*, Vahid Ghasem Amooeian and Ehsan Rashidi
DOI: 10.2174/1566523218666180302163029

Gene Therapy in Kidney Transplantation: Evidence of Efficacy and Future Directions

Volume: 17   Issue: 6
Pp: 434-441
Jiawei Li, Guisheng Qi, Guowei Tu, Cheng Yang* and Ruiming Rong*
DOI: 10.2174/1566523218666180214095606

A New Era for Hemoglobinopathies: More Than One Curative Option

Volume: 17   Issue: 5
Pp: 364-378
Nikoletta Psatha, Penelope-Georgia Papayanni and Evangelia Yannaki*
DOI: 10.2174/1566523218666180119123655

Therapeutic Applications of CRISPR/Cas for Duchenne Muscular Dystrophy

Volume: 17   Issue: 4
Pp: 301-308
Tatianna Wai Ying Wong and Ronald D. Cohn*
DOI: 10.2174/1566523217666171121165046

Challenges and Advances in Gene Therapy Approaches for Neurodegenerative Disorders

Volume: 17   Issue: 3
Pp: 187-193
Aneesh Donde, Philip C. Wong and Liam L. Chen*
DOI: 10.2174/1566523217666171013124150

Mesenchymal Stem Cell-derived Extracellular Vesicles for Renal Repair

Volume: 17   Issue: 1
Pp: 29-42
Arash Aghajani Nargesi, Lilach O. Lerman and Alfonso Eirin*
DOI: 10.2174/1566523217666170412110724

Seq and You Will Find

Volume: 16   Issue: 3
Pp: 220-229
Nicole Schonrock, Nicky Jonkhout and John S. Mattick
DOI: 10.2174/1566523216666160524144159

Gene Electrotransfer: A Mechanistic Perspective open access plus

Volume: 16   Issue: 2
Pp: 98-129
Christelle Rosazza, Sasa Haberl Meglic, Andreas Zumbusch, Marie-Pierre Rols and Damijan Miklavcic
DOI: 10.2174/1566523216666160331130040

Rational Autologous Cell Sources For Therapy of Heart Failure - Vehicles and Targets For Gene and RNA Therapies

Volume: 16   Issue: 1
Pp: 21-33
Milla Lampinen, Antti Vento, Jari Laurikka, Johanna Nystedt, Eero Mervaala, Ari Harjula and Esko Kankuri
DOI: 10.2174/1566523216666160104141809

Contemporary Animal Models For Human Gene Therapy Applications

Volume: 15   Issue: 6
Pp: 531-540
Chitra Gopinath, Trupti Job Nathar, Arkasubhra Ghosh, Dennis Durand Hickstein and Everette Jacob Remington Nelson
DOI: 10.2174/1566523215666150929110424

miR-122 is a Unique Molecule with Great Potential in Diagnosis, Prognosis of Liver Disease, and Therapy Both as miRNA Mimic and Antimir promotion: free to download

Volume: 15   Issue: 2
Pp: 142-150
Sharda Thakral and Kalpana Ghoshal
DOI: 10.2174/1566523214666141224095610

Preclinical Evaluation of Efficacy and Safety of an Improved Lentiviral Vector for the Treatment of β-Thalassemia and Sickle Cell Disease open access plus

Volume: 15   Issue: 1
Pp: 64-81
Olivier Negre, Cynthia Bartholomae, Yves Beuzard, Marina Cavazzana, Lauryn Christiansen, Celine Courne, Annette Deichmann, Maria Denaro, Edouard de Dreuzy, Mitchell Finer, Raffaele Fronza, Beatrix Gillet-Legrand, Christophe Joubert, Robert Kutner, Philippe Leboulch, Leila Maouche, Anais Paulard, Francis J. Pierciey, Michael Rothe, Byoung Ryu, Manfred Schmidt, Christof von Kalle, Emmanuel Payen and Gabor Veres
DOI: 10.2174/1566523214666141127095336

Gene Therapy for Wiskott-Aldrich Syndrome

Volume: 14   Issue: 6
Pp: 413-421
Marita Bosticardo, Francesca Ferrua, Marina Cavazzana and Alessandro Aiuti
DOI: 10.2174/1566523214666140918103731