Current Gene Therapy

Editor-in-Chief:

Lung-Ji Chang
University of Florida
Gainesville, FL
USA

 

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Editorial (Thematic Issue):Stem Cell-Based and Gene Therapy for Hereditary Muscle Disorders free to download

Volume:15   Issue:4
Pp: 327-328
Marinee K. Chuah
DOI: 10.2174/156652321504150722121542

Therapeutic Approaches for Dominant Muscle Diseases: Highlight on Myotonic Dystrophy

Volume:15   Issue:4
Pp: 329-337
A. F. Klein, S. Dastidar, D. Furling and M. K. Chuah
DOI: 10.2174/1566523215666150630120537

Preclinical Development of New Therapy for Glycogen Storage Diseases

Volume:15   Issue:4
Pp: 338-347
Baodong Sun, Elizabeth D. Brooks and Dwight D. Koeberl
DOI: 10.2174/1566523215666150630132253

Adult Stem Cells and Skeletal Muscle Regeneration

Volume:15   Issue:4
Pp: 348-363
Domiziana Costamagna, Emanuele Berardi, Gabriele Ceccarelli and Maurilio Sampaolesi
DOI: 10.2174/1566523215666150630121024

Pluripotent Stem Cells for Gene Therapy of Degenerative Muscle Diseases

Volume:15   Issue:4
Pp: 364-380
Mariana Loperfido, Heather B. Steele-Stallard, Francesco Saverio Tedesco and Thierry VandenDriessche
DOI: 10.2174/1566523215666150630121207

Adeno-Associated Virus (AAV) Mediated Dystrophin Gene Transfer Studies and Exon Skipping Strategies for Duchenne Muscular Dystrophy (DMD)

Volume:15   Issue:4
Pp: 395-415
Klaudia Kawecka, Michael Theodoulides, Yalin Hasoglu, Susan Jarmin, Hanna Kymalainen, Anita Le-Heron, Linda Popplewell, Alberto Malerba, George Dickson and Takis Athanasopoulos
DOI: 10.2174/1566523215666150710123830

Successful Combination of Sequential Gene Therapy and Rescue Allo-HSCT in Two Children with X-CGD - Importance of Timing

Volume:15   Issue:4
Pp: 416-427
Ulrich Siler, Anna Paruzynski, Heidi Holtgreve-Grez, Elena Kuzmenko, Ulrike Koehl, Eleonore D. Renner, Canan Alhan, Arjan A. van de Loosdrecht, Joachim Schwäble, Thomas Pfluger, Joelle Tcinda9, Markus Schmugge, Anna Jauch, Sonja Naundorf, Klaus Kühlcke, Gundula Notheis, Tayfun Güngör, Christof V. Kalle, Manfred Schmidt, Manuel Grez, Reinhard Seger and Janine Reichenbach*
DOI: 10.2174/1566523215666150515145255

Gene Manipulation of Human Embryonic Stem Cells by In Vitro-Synthesized mRNA for Gene Therapy

Volume:15   Issue:4
Pp: 428-435
Xiao Li Wang, Li Yu, Yan Ding, Xing Rong Guo, Ya Hong Yuan and Dong Sheng Li
DOI: 10.2174/1566523215666150515144533

A Simple High Efficiency Intra-Islet Transduction Protocol Using Lentiviral Vectors open access plus

Volume:15   Issue:4
Pp: 436-446
Carmen Maria Jimenez-Moreno, Irene de Gracia Herrera-Gomez, Livia Lopez-Noriega, Petra Isabel Lorenzo, Nadia Cobo-Vuilleumier, Esther Fuente-Martin, Jose Manuel Mellado-Gil, Geraldine Parnaud, Domenico Bosco, Benoit Raymond Gauthier and Alejandro Martin-Montalvo
DOI: 10.2174/1566523215666150630121557