Current Gene Therapy


Liang Cheng
College of Bioinformatics Science and Technology
Harbin Medical University
Harbin, Heilongjiang


Become EABM
Become Reviewer

Editorial [Hot Topic: Therapeutic Approaches to Muscular Dystrophies] promotion: free to download

Volume:12   Issue: 3
Pp: 137-138
Aurelie Goyenvalle
DOI: 10.2174/156652312800840568

Gene Replacement Therapies for Duchenne Muscular Dystrophy Using Adeno-Associated Viral Vectors

Volume:12   Issue: 3
Pp: 139-151
Jane T. Seto, Julian N. Ramos, Lindsey Muir, Jeffrey S. Chamberlain and Guy L. Odom
DOI: 10.2174/156652312800840603

Antisense Oligonucleotide-Mediated Exon Skipping for Duchenne Muscular Dystrophy: Progress and Challenges open access plus

Volume:12   Issue: 3
Pp: 152-160
Virginia Arechavala-Gomeza, Karen Anthony, Jennifer Morgan and Francesco Muntoni
DOI: 10.2174/156652312800840621

Use of Cell-Penetrating-Peptides in Oligonucleotide Splice Switching Therapy

Volume:12   Issue: 3
Pp: 161-178
Samir A. El Andaloussi, Suzan M. Hammond, Imre Mager and Matthew J.A. Wood
DOI: 10.2174/156652312800840612

Splicing Modulation Mediated by Small Nuclear RNAs as Therapeutic Approaches for Muscular Dystrophies open access plus

Volume:12   Issue: 3
Pp: 179-191
Rachid Benchaouir and Aurelie Goyenvalle
DOI: 10.2174/156652312800840586

The Role of Stem Cells in Muscular Dystrophies

Volume:12   Issue: 3
Pp: 192-205
Mirella Meregalli, Andrea Farini, Federica Colleoni, Letizia Cassinelli and Yvan Torrente
DOI: 10.2174/156652312800840559

Pharmacologically Targeting the Primary Defect and Downstream Pathology in Duchenne Muscular Dystrophy

Volume:12   Issue: 3
Pp: 206-244
Rebecca J. Fairclough, Kelly J. Perkins and Kay E. Davies
DOI: 10.2174/156652312800840595